The advances and challenges of Gene Therapy for Duchenne Muscular Dystrophy
Since the discovery of the dystrophin gene (DMD gene) thirty years ago, several therapeutic approaches have been investigated to treat Duchenne muscular dystrophy (DMD). This includes cell therapy, exon jumping, exonic knockout, and the CinDel ...
Read Full Article HTML DOI: 10.29328/journal.jgmgt.1001003 Views: 4869 0
Progress in the development of Lipoplex and Polyplex modifi ed with Anionic Polymer for effi cient Gene Delivery
Nucleic acid-based therapy has become an increasingly important strategy for treating a variety of human diseases. In systemic therapy, a therapeutic gene must be delivered effi ciently to its target tissues without side effects. To deliver a t...
Read Full Article HTML DOI: 10.29328/journal.jgmgt.1001002 Views: 2113 0
CRISPR genome editing: A general view
CRISPR technology has presented a path forward for genomic engineering and gene modification. The framework for the use of CRISPR technology to manipulate the human genome is of great interest and the form of its development and application has...
Read Full Article HTML DOI: 10.29328/journal.jgmgt.1001001 Views: 2103 0
Welcome to Genetic Medicine and Gene Therapy Journal
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Since the discovery of the dystrophin gene (DMD gene) thirty years ago, several therapeutic approaches have been investigated to treat Duchenne muscular dystrophy (DMD). This includes cell thera...
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Nucleic acid-based therapy has become an increasingly important strategy for treating a variety of human diseases. In systemic therapy, a therapeutic gene must be delivered effi ciently to its t...
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CRISPR technology has presented a path forward for genomic engineering and gene modification. The framework for the use of CRISPR technology to manipulate the human genome is of great interest a...